Gene Therapy and Sly Syndrome: Could This Be a Cure?
What Is Sly Syndrome? Imagine navigating life without a road map — that’s what families often face when their child is diagnosed with a rare condition like Sly Syndrome, also known as Mucopolysaccharidosis Type VII (MPS VII). It’s an inherited disorder, caused by a deficiency of the beta-glucuronidase enzyme, leading to the accumulation of harmful substances in...
0 Comments 0 Shares